IQVIA™ Real-World Insights Bibliography

Cost-utility analysis of life-long prophylaxis with recombinant factor VIIIFc vs recombinant factor VIII for the management of severe hemophilia A in Sweden.
Author(s): Henry N1, Jovanović J1, Schlueter M1, Kritikou P2, Wilson K2, Myrén KJ2.
Affiliations(s): Henry N1, Jovanović J1, Schlueter M1, Kritikou P2, Wilson K2, Myrén KJ2. 1 IQVIA , London , UK. 2 Swedish Orphan Biovitrum AB , Stockholm , Sweden.
Publication(s): 
Document Type(s): Article,
Countries: UK,
C:
Y:
Hematology, Rare disease,
2018
  L:
A:
English
Retrospective database analysis,
  Add to report
 
 
Angiotensin II receptor blockers and intestinal malabsorption: an observational cohort study in Germany and Italy
Author(s): Malfertheiner P1, Heiman F2, Ripellino C3, Cataldo N2
Affiliations(s): 1 Otto-von-Guericke Universität, Klinik für Gastroenterologie, Hepatologie und Infektiologie 2 QuintilesIMS, Milan, Italy 3 HEOR Consultant, Freelance, Milan, Italy
Publication(s):  ISPOR 20th Annual European Congress, 4-8 November 2017, Glasgow, Scotland
Document Type(s): Poster,
Countries: Germany, Italy,
C:
Y:
Drug safety, Gastrointestinal disorders, Rare disease,
2017
  L:
A:
English
Database Study, Epidemiological study, Longitudinal study, Observational study, Population Based Study, Real World Data, Real World Evidence, Retrospective cohort analysis, Retrospective database analysis,
  Add to report
 
 
Real-world Assessment of Renal Involvement in Tuberous Sclerosis Complex (TSC) Patients in the United Kingdom (UK): A Retrospective Cohort Study in the Clinical Practice Research Datalink (CPRD)
Author(s): Kingswood, Chris1, Nasuti, Paola2, Demuth, Dirk2, Patel, Keyur2, Myland, Melissa2, Erhard, Clement3, Gray, Elizabeth4, Pinnegar, Alun4, Magestro, Matthew5
Affiliations(s): The Royal Sussex County Hospital, Brighton, England 2 IMS Health, London, UK 3 CE Analytics, Cambridge, UK 4 Novartis Pharmaceuticals UK Ltd, Frimley, UK 5 Novartis Pharmaceuticals Corporation, East Hanover NJ, USA
Publication(s):  International TSC Research Conference (Windsor, 11th Sept 2015).
Document Type(s): Poster,
Countries: England,
C:
Y:
Oncology, Pediatrics, Rare disease,
2015
  L:
A:
English
Retrospective cohort analysis,
  Add to report
 
 
Association of sweat chloride concentration at time of diagnosis and CFTR genotype with mortality and cystic fibrosis phenotype
Author(s): McKone EF, Goss C, Velentgas P, Swenson A
Affiliations(s): 
Publication(s):  Journal of Cystic Fibrosis. JCF1155. Feb 2015. 10.1016(j.jcf.2015) 01.005
Document Type(s): Article,
Countries: 
C:
Y:
Rare disease,
2015
  L:
A:
English
RWLPR (Real-World Late Phase Research-quintiles,
  Add to report
 
 
Fifth interim analysis of the Kuvan® Adult Maternal Paediatric European Registry (KAMPER): Insights into management/practice in patients with PKU.
Author(s): Lagler FB, Muntau AC, Feillet F, Rogoff D, Moreau-Stucker F, Alm J, Burlina A, Trefz FK.
Affiliations(s): Quintiles Real-World and Late Phase Research
Publication(s):  Society for the Study of Inborn Errors of Metabolism (SSIEM) Annual Congress, 1–4 September 2015, Lyon, France, Abstract No. P-160
Document Type(s): Abstract,
Countries: 
C:
Y:
Patient Registries & Real-World Study Methods, Rare disease,
2015
  L:
A:
English
RWLPR (Real-World Late Phase Research-quintiles,
  Add to report
 
 
Impact of Acute Bleeding on Daily Activities of Patients with Congenital Hemophilia with Inhibitors and Their Caregivers and Families: Observations from the Dosing Observational Study in Hemophilia (DOSE). Science Direct
Author(s): Recht N, Neufeld EJ, Sharma VR, Solem CT, Pickard S, Gut RZ, MD, Cooper DL
Affiliations(s): 
Publication(s): 
Document Type(s): Article,
Countries: 
C:
Y:
Rare disease,
2014
  L:
A:
English
RWLPR (Real-World Late Phase Research-quintiles,
  Add to report
 
 
The Budget Impact of Orphan Drugs in the U.S.: A 2007-2013 MIDAS Sales Data Analysis
Author(s): Victoria Divino, Mitch Dekoven, Weiying Wang, Michael Kleinrock, R. Donald Harvey, Rolin L Wade, and Satyin Kaura
Affiliations(s): Celgene, IMS authors: Victoria Divino, Mitch Dekoven, Michael Kleinrock, Rolin L Wade
Publication(s):  2014 American Society of Hematology (ASH) Annual Meeting
Document Type(s): Oral presentation,
Countries: USA,
Click here for the abstract
C:
Y:
Rare disease,
2014
  L:
A:
English
Budget impact,
  Add to report
 
 
Health-related Quality of Life in Patients with Hemophilia and Inhibitors on Prophylaxis with an Activated Prothrombin Complex Concentrate: Results From the Pro-FEIBA Study
Author(s): Gringeri A, Leissinger C,,Cortesi P, Jo H, Fusco F, Riva F, Bulent A, Berntorp E, Carpenter S, Kavakli K, Morfini M, Negrier C, Rocino A, Schramm W, Uscatescu M, Windyga J, Zulfikar B, Mantovani LG
Affiliations(s): 
Publication(s):  Haemophilia 2013 Sep;19(5):736-43
Document Type(s): Article,
Countries: 
C:
Y:
Rare disease,
2013
  L:
A:
English
RWLPR (Real-World Late Phase Research-quintiles,
  Add to report
 
 
Impact of pregnancy on women with cystic fibrosis
Author(s): McMullen AH, Pasta DJ, Frederick PD, Konstan MW, Morgan WJ, Schechter MS, Wagener JS
Affiliations(s): 
Publication(s):  Chest 2006; 129(3):706-711
Document Type(s): Article,
Countries: 
C:
Y:
Rare disease,
2006
  L:
A:
English
RWLPR (Real-World Late Phase Research-quintiles,
  Add to report